Rare Disease Day: Why it matters and how to get involved
Rare Disease Day 2025 aims to uplift the rare disease community and promote greater awareness.
Rare Disease Day 2025 aims to uplift the rare disease community and promote greater awareness.
Analysis of data from the trial suggested that outpatient heart failure should be an endpoint in future clinical studies for ATTR-CM.
A study found that patients with ATTR-CM who underwent heart transplantation experienced survival rates similar to patients without it.
A case report emphasized the challenges of diagnosing transthyretin amyloid cardiomyopathy (ATTR-CM) and the need for early intervention.
A study found that tafamidis may reduce levels of a diagnostic marker of ATTR-CM, but the effects appear to plateau over time.